DelveInsight’s, “Metachromatic Leukodystrophy Pipeline Insight 2023” report provides comprehensive insights about 6+ companies and 6+ pipeline drugs in the Metachromatic Leukodystrophy pipeline landscape. It covers the Metachromatic Leukodystrophy pipeline drug profiles, including clinical and nonclinical stage products. It also covers the Metachromatic Leukodystrophy therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.
Key Takeaways from the Metachromatic Leukodystrophy Pipeline Report
- DelveInsight’s Metachromatic Leukodystrophy pipeline report depicts a robust space with 6+ active players working to develop 6+ pipeline therapies for Metachromatic Leukodystrophy treatment.
- The leading companies working in the Metachromatic Leukodystrophy Market include Takeda, Denali Therapeutics, Orchard Therapeutics, Homology Medicines, Passage Bio, ArmaGen Technologies, and others.
- Promising Metachromatic Leukodystrophy Pipeline Therapies in the various stages of development include SHP611, HGT-1110, OTL-200, rhARSA, MGTA-456, and others.
- June 2023: Shire announced a study of phase 2 clinical trials for SHP611. The main aim of the study is to determine if SHP611 given by injection into the spinal fluid that surrounds the brain and spinal cord (intrathecal; IT) prolongs the time for children with Metachromatic Leukodystrophy (MLD) to retain the ability to move from place to place. Other aims of the study are to determine the effects of intrathecal administration of SHP611 on movement and speech functions and to learn how well SHP611 injected in the spinal fluid that surrounds the brain and spinal cord is tolerated.
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In the Metachromatic Leukodystrophy pipeline report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Metachromatic Leukodystrophy collaborations, licensing, mergers and acquisition, funding, designations and other product related details.
Metachromatic Leukodystrophy Overview
Metachromatic leukodystrophy (MLD) is a rare hereditary disease characterized by accumulation of fats called sulfatides. This causes the destruction of the protective fatty layer (myelin sheath) surrounding the nerves in both the central nervous system and the peripheral nervous system. There are three types of MLD based on the age symptoms appear: late-infantile MLD, juvenile MLD, and adult MLD.
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Metachromatic Leukodystrophy Emerging Drugs Profile
- OTL-200: Orchard Therapeutics
- TAK-611: Takeda
Metachromatic Leukodystrophy Pipeline Therapeutics Assessment
There are approx. 6+ key companies which are developing the Metachromatic Leukodystrophy. The Metachromatic Leukodystrophy companies which have their Metachromatic Leukodystrophy drug candidates in the most advanced stage, i.e. Registered include, Orchard Therapeutics.
Learn more about the emerging Metachromatic Leukodystrophy Pipeline Therapies @ Metachromatic Leukodystrophy Clinical Trials Assessment
Scope of the Metachromatic Leukodystrophy Pipeline Report
- Coverage- Global
- Metachromatic Leukodystrophy Therapeutic Assessment by Product Type: Mono, Combination, Mono/Combination
- Metachromatic Leukodystrophy Therapeutic Assessment by Clinical Stages: Discovery, Pre-clinical, Phase I, Phase II, Phase III
- Metachromatic Leukodystrophy Companies- Takeda, Denali Therapeutics, Orchard Therapeutics, Homology Medicines, Passage Bio, ArmaGen Technologies, and others.
- Metachromatic Leukodystrophy Pipeline Therapies- SHP611, HGT-1110, OTL-200, rhARSA, MGTA-456, and others.
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Table of Content
- Introduction
- Executive Summary
- Metachromatic Leukodystrophy: Overview
- Pipeline Therapeutics
- Therapeutic Assessment
- Metachromatic Leukodystrophy– DelveInsight’s Analytical Perspective
- In-depth Commercial Assessment
- Metachromatic Leukodystrophy Collaboration Deals
- Late Stage Products (Phase III)
- Drug Name: Company Name
- Drug profiles in the detailed report…..
- Mid Stage Products (Phase II)
- TAK-611: Takeda
- Drug profiles in the detailed report…..
- Early Stage Products (Phase I)
- Drug Name: Company Name
- Drug profiles in the detailed report…..
- Preclinical and Discovery Stage Products
- PBML-04: Passage Bio
- Drug profiles in the detailed report…..
- Inactive Products
- Metachromatic Leukodystrophy Key Companies
- Metachromatic Leukodystrophy Key Products
- Metachromatic Leukodystrophy- Unmet Needs
- Metachromatic Leukodystrophy- Market Drivers and Barriers
- Metachromatic Leukodystrophy- Future Perspectives and Conclusion
- Metachromatic Leukodystrophy Analyst Views
- Metachromatic Leukodystrophy Key Companies
- Appendix
For further information on the Metachromatic Leukodystrophy Pipeline therapeutics, reach out to Metachromatic Leukodystrophy Unmet Needs and Analyst Views
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